Register Now
Why register?
 The leading web portal for pharmacy resources, news, education and careers November 20, 2017
Pharmacy Choice - Pharmaceutical News - CureDuchenne Applauds the FDA Approval of Marathon's EMFLAZA (deflazacort) for the Treatment of Duchenne Muscular Dystrophy - November 20, 2017

Pharmacy News Article

 2/13/17 - CureDuchenne Applauds the FDA Approval of Marathon's EMFLAZA (deflazacort) for the Treatment of Duchenne Muscular Dystrophy

Release date- 09022017 - NEWPORT BEACH, Calif- CureDuchenne applauds the U.S. Food and Drug Administration (FDA) approval of EMFLAZA (deflazacort), developed by Marathon Pharmaceuticals, the first drug in the U.S. approved for use by patients five and older with Duchenne muscular dystrophy regardless of genetic mutation.

EMFLAZA is a corticosteroid that demonstrates anti-inflammatory and immunosuppressant effects. Clinically, EMFLAZA has meaningful benefits in treating patients with Duchenne. Those treated with EMFLAZA showed improved muscle strength and showed slower decline in functional ability. Learn more about EMFLAZA here.

'For the first time all those impacted by Duchenne muscular dystrophy have a FDA-approved treatment available to them,' said Debra Miller, Founder and CEO of CureDuchenne. 'This is a milestone for the Duchenne community to have access to this therapy that shows improved muscle strength and slower decline in functional ability. As a mother of a young man with Duchenne, deflazcort has been an important part of my son's standard of care since he was diagnosed. We are delighted that Marathon Pharmaceuticals is committed to providing access to the drug with a comprehensive patient assistance program.'

Duchenne is a fatal genetic disease that causes muscle degeneration. Patients are usually diagnosed by age 5, most lose their ability to walk in the teens and most don't survive their mid-20s.

'This treatment provides hope for families impacted by Duchenne,' said Miller. 'We need to continue to extend and improve the lives of those affected by Duchenne by funding research that will help treat all aspects of the disease until there is a cure.'

About CureDuchenne

CureDuchenne is the leading nonprofit focused on funding research to find a cure for Duchenne muscular dystrophy, a disease that affects more than 300,000 boys worldwide. CureDuchenne's mission is to extend and improve the lives of those affected by Duchenne. With support from CureDuchenne, nine research projects have advanced to human clinical trials. CureDuchenne provides the Duchenne community with resources on the best standard of care through its CureDuchenne Cares program. For more information, please visit and follow us on Facebook, Twitter, Instagram and YouTube.

(c) 2017 Electronic News Publishing -

Pharmacy News Index
  Drug Delivery Systems
  FDA Final Approvals
  Front Page Healthcare News
  Generic Drugs
  Hospital Industry
  Internet Pharmacy
  IT in Healthcare
  Medicare & Medicaid
  Over-the-Counter Drugs
  Pharm Industry Trends and Policy
  Pharmaceutical Development
  Pharmaceutical Industry


Last Chance
Nov 20: Obesity Management: Overview of Pharmacotherapy
Last Chance
Nov 21: Standards of Practice for Filling Controlled Substance Prescriptions in Florida
Last Chance
Nov 22: Medical Marijuana: Examining the Science, Not the Politics
Nov 27: Drug Diversion and the Law: Updates and Considerations
Nov 28: An Integrative Approach to Managing Arthritis
Click for entire Webinar Calendar

Special Announcement

Free Membership
Enjoy Drug Search, industry newsletters and more...

Nursing Jobs
Are you a nurse looking for a job?

Check out the Nursing Job Source.

Your number one choice for nursing jobs.

Websites »
Copyright © 2017 Pharmacy Choice - All rights reserved.
Terms and Conditions | Privacy Statement